Sep 30, 2019
Girl Diagnosed with Fatal Brain Disease Gets a Tailor-Made Drug within a Year
When Mila Makovec was diagnosed with a rare neurological condition at age 6, her prognosis was grim. The condition, known as Batten disease, is fatal, with death usually occurring in late childhood or the early teen years. There is no cure, and at the time of Mila's diagnosis, in 2016,...